Rare Disease Research Embraces The Unknown. Let's Take It On. Together.

Over 10,000 rare diseases affect an estimated 400 million people worldwide, and 95% of them do not have a suitable cure. In the complex and uncharted territory of rare disease research, particularly cell and gene studies, Premier Research offers significant experience with natural history studies, precision medicine, and real-world data planning, trial design, and regulatory strategy to guide rare disease product development.

Partnered with Premier’s strong expertise in enrolling special patient populations and its ability to manage complicated logistics and CMC challenges, the company strives to provide sponsors of novel rare disease therapies with proactive solutions to ensure trials stay on course.

Discover how Premier’s deep expertise in rare diseases and rare oncology is accelerating clinical development to transform data into life-changing therapies for patients who need them most.