Charting The Path: How Patient And Caregiver Journeys Guide Rare Disease Study Design

By Kris O'Brien

Teams who want to be successful in rare disease development programs know that putting the patients first is a crucial aspect of the study. A common concern that comes up, though, is being able to determine how much patient input can be integrated into the study design without compromising the security of high-quality data.

Although a bit of a balancing act, it is possible to design a study that will successfully meet endpoints while making participation easier for both patients and caregivers. It starts with understanding the patient and caregiver journeys, and identifying their challenges and needs to ensure studies are designed with these factors in mind. This patient-centric approach helps sponsors not only optimize product design and value but also enhance clinical trial recruitment and retention.

Discover how designing trials that account for both patient and caregiver needs can improve the overall experience of study participation and may contribute to improved patient retention and higher-quality data.