White Paper

Natural History Studies For Rare Diseases: Development Strategies For External Comparator Arms Leveraging Real World Insights

By Emily Bratton, PHD, MSPH,Cassie Holt, PHD, MPH, CPH, Sarah Kromrey, PHD, Jeffrey Keefer, MD, PHD

Doctor

This paper explores essential principles for defining the right strategy for natural history studies and how to design such studies in a way that the data can be used as an external comparator to augment future regulatory filings and payer submissions. For more information, download the available white paper.

access the White Paper!

Get unlimited access to:

Trend and Thought Leadership Articles
Case Studies & White Papers
Extensive Product Database
Members-Only Premium Content
Welcome Back! Please Log In to Continue. X

Enter your credentials below to log in. Not yet a member of Clinical Leader? Subscribe today.

Subscribe to Clinical Leader X

Please enter your email address and create a password to access the full content, Or log in to your account to continue.

or

Subscribe to Clinical Leader