Site Selection Solutions Using Patient Insights For Rare Disease Trials

Rare disease trials face unique recruitment challenges, and traditional site selection methods often fail to capture where patients actually receive care. A more effective approach combines data-driven analysis with physician outreach and direct engagement from patient advocacy organizations to uncover treatment patterns, identify overlooked sites, and understand the real-world patient journey.

Drawing on practical case studies, experts explore a three-pillar framework that integrates data intelligence, physician-to-physician discussions, and patient community insights to inform feasibility assessments and site selection strategies. This patient-centered methodology helps sponsors move beyond published literature and historical trial data to gain a clearer view of patient populations, enrollment potential, protocol feasibility, and retention risks.

The discussion highlights how local advocacy groups can reveal hidden referral networks, validate patient availability, and provide cultural and logistical insights that improve trial accessibility. Speakers also examine the growing role of AI and real-world data in landscape analysis, while emphasizing the continued importance of human expertise and community relationships.

Watch the full webinar to learn how patient insights can transform rare disease site selection and support more efficient, inclusive, and successful clinical trials.